Patient Advocacy
About Patient Advocacy at Fulcrum
We acknowledge the significant unmet
medical need faced by people living with sickle
cell disease (SCD) and their families.
Build Trust
Engage Communities
Support Access
Amplify Voices
Partnering with the Sickle Cell Community
Engaging in dialogue
Regular collaboration with the SCD community to understand needs and priorities.
Maintaining presence
Active participation at patient conferences, community events, and professional societies.
Supporting policy advocacy
Partnering with patient organizations to improve access and outcomes.
Integrating patient perspectives
Throughout our drug development process—from clinical trial design to access planning.
Our Team
Meet the dedicated professionals leading Fulcrum’s patient advocacy efforts.
Advocacy & Policy
ensuring patient voices are central to our work in
sickle cell disease and beyond.
Marjorie develops and implements patient-centered strategies that strengthen Fulcrum’s partnerships with the SCD community.
Patient Voices
Hear from members of the sickle cell community about their experiences, challenges, and hopes for the future.
Patient Voices
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SCD Resources
Access information about sickle cell disease, clinical research, and community support.
Exploring New Research in Sickle Cell Disease: Fulcrum Updates from the Pioneer Study.
Clinical Data Presentation (September 2025)
Learn about the promising results from our PIONEER study, featuring insights from Fulcrum leadership and leading sickle cell specialists Dr. Shenya Allen (Inova Fairfax) and Dr. Wally Smith (Virginia Commonwealth University).
Pociredir, a Novel Oral Once-Daily Fetal Hemoglobin Inducer
Results from the phase 1B PIONEER study in adult participants with severe sickle cell disease and hydroxyurea intolerance or unresponsiveness.
A Strategic Partnership to Accelerate Sickle Cell Emergency Care
Three-year collaboration is aimed at enhancing a key aspect of sickle cell management: expediting care during a pain crisis
Information on Clinical Trials
Contact Us
Patients or caregivers who are interested in learning more about Fulcrum Therapeutics and our programs can contact us at the email below. For medical advice, please contact your physician.